rare disease Related News
New therapy could revolutionise treatment for fatal Sanfilippo Syndrome
A new combination therapy could revolutionise treatment for children living with a rare and fatal lysosomal storage disorder called Sanfilippo Syndrome.
GlycoNet researchers are using...
Improving access to gene and cell therapies for people with rare diseases
A new report has addressed challenges to accessing gene and cell therapies for people living with rare diseases.
EURORDIS-Rare Diseases Europe and the partners of the...
MPS disease: the health benefits of cannabinoids to MPS patients
Over the last few decades, the health benefits of cannabinoids has become an increasingly popular topic, but can this help those with the rare...
Introducing the Narrenturm: the world’s first hospital for the mentally ill
Before the end of the 18th century, those who were mentally ill were not regarded as patients, however in 1784 Austria, the Narrenturm was...