cell and gene therapy Related News
NHS to deliver world-first national genetic screening service for children
The NHS will introduce a groundbreaking genetic screening service hailed as the start of a “new era of genomic medicine”.
At the first-ever NHS genomics...
Stem cell and gene therapy shows promise in motor neuron disease trial
Cedars-Sinai investigators have developed a stem cell and gene therapy combination that potentially protects against motor neuron disease.
Motor neurone disease (MND), also known as...
Using ultra-low freezers to maintain the viability of cell and gene therapy products
B Medical Systems explain how their ultra-low freezers can offer valuable cold chain solutions for the burgeoning cell and gene therapy market.
Many cell and...
Gene therapy for achromatopsia in children partly restores cone function
A new study by University College London has found gene therapy for achromatopsia in children partly restored cone function.
Achromatopsia is a rare inherited condition...
Scientists to rewrite DNA to cure inherited heart muscle conditions
Researchers have developed an injectable cure for inherited heart muscle conditions that can kill young people.
An international team of researchers were recently announced as...
Reducing bleeding risk for haemophilia B patients with gene therapy
Scientists have developed a single gene therapy injection that could reduce bleeding risk in haemophilia B patients.
Scientists from University College London (UCL), Royal Free...
Promising therapy for recombination-deficient severe combined immunodeficiency
Recomb outlines important milestones in the development of autologous haematopoietic stem cell-based gene therapy for recombination-deficient severe combined immunodeficiency.
Infants born with severe combined immunodeficiency...
A step closer to gene therapy that restores hearing for congenitally deaf
Findings from a new study have brought the possibility of gene therapy that could restore hearing in the congenitally deaf one step closer.
Mutations in...
Hope for rare disease patients: an approach to funding gene therapy
Roger Johansson, Vice President and General Manager – Northern Europe with the global biopharmaceutical company PTC Therapeutics, discusses the need to establish an environment...
Combining machine learning and cell engineering for cancer therapies
Scientists are tackling the ‘Holy Grail’ of oncology by combing machine learning and cell engineering to create ‘living medicines’ that precisely target cancer tumours.
Scientists...
Non-hereditary mutation acts as natural gene therapy for GATA2 deficiency
Scientists have identified a non-inherited mutation in blood cells from a patient with GATA2 deficiency that may have prevented bone marrow failure and other...
Tumour-tropic liposome technology could pave way for cancer treatments
A collaboration between Toshiba and Shinshu University has resulted in the development of a ‘tumour-tropic liposome technology’ for gene therapy that could pave the...
Mitchell disease: solving the medical mystery
Scientists have uncovered a genetic mutation that links to the rare Mitchell disease.
A team of researchers led by Dr Hugo Bellen at Baylor College...
Gene therapy may hold key to treating life-threatening Danon disease
A new study has found that gene therapy improved cardiac, muscle and liver function in Danon disease mouse models.
Danon disease is a very rare,...
edu-BRoTHER: an innovative student exchange programme providing biobank skills
University Regensburg Professor Christoph Brochhausen showcases the edu-BRoTHER biobanking student exchange project
Biobanks are an increasingly significant resource in healthcare research. Professor Christoph Brochhausen, of...
NUI Galway launch €7.45m research project into osteoarthritis
The EU Horizon 2020 project will research the robotic production of groundbreaking regenerative stem cell therapies
The €7.45m AutoCRAT project will enable researchers to develop...
Space, neurogenetics and nervous system research
Have you ever wondered about how space alters the mechanics of human muscles? Health Europa Quarterly spoke with Bertrand Fontaine, Director of the Institute...
The dawn of gene therapy for rare diseases
Andrew Obenshain, Chief of Wings at biotechnology firm bluebird bio, tells HEQ about the future of gene therapies in the treatment of rare diseases
Up...
bluebird bio announces launch of beta thalassaemia gene therapy in Germany
Zynteglo is a one-time gene therapy that addresses the underlying genetic cause of TDT and offers patients the potential to become transfusion independent.
The one-time...
Mother Nature provides new gene therapy strategy to reverse disease
Scientists have developed a new gene therapy technique by transforming human cells into mass producers of tiny nano-sized particles full of genetic material that...